PTC Therapeutics, Inc.
Dyne Therapeutics, Inc.
Biohaven Pharmaceutical Holding Company Ltd.
Alkermes plc
Intra-Cellular Therapies, Inc.
Catalyst Pharmaceuticals, Inc.
Xenon Pharmaceuticals Inc.
ACADIA Pharmaceuticals Inc.
Axonics, Inc.
Biogen
Sarepta Therapeutics, Inc.
Neurocrine Biosciences
Supernus Pharmaceuticals, Inc.
Edgewise Therapeutics, Inc.
Cassava Sciences, Inc.
Avadel Pharmaceuticals plc
Longboard Pharmaceuticals, Inc.
Integra LifeSciences Holdings Corporation
Praxis Precision Medicines, Inc.
Prothena Corporation plc
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